
Fresh off first FDA approval, Amicus spends $100M to acquire 10 gene therapies
The company acquired 10 AAV-based gene therapies in development for lysosomal storage disorders, including two already in early clinical trials.
The company acquired 10 AAV-based gene therapies in development for lysosomal storage disorders, including two already in early clinical trials.
The Boston-based startup hopes to advance its products into clinical trials in the next 2-3 years, CEO says.
AstraZeneca subsidiary and California-based firm to develop AAV-based therapy for chronic lung disease.